Novel CRISPR-Cas9-Based Promising in ATTR Cardiomyopathy

Watchdoq November 17, 2024
(MedPage Today) -- CHICAGO – A CRISPR-Cas9-based investigational therapy was linked with a drop in serum transthyretin (TTR) levels in patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM), according to phase I data.
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